Research of the Month

CRISPR-Cas9–mediated therapeutic editing of Rpe65 ameliorates the disease phenotypes in a mouse model of Leber congenital amaurosis

Dong Hyun Jo1*, Dong Woo Song2*, Chang Sik Cho1, Un Gi Kim2, Kyu Jun Lee2, Kihwang Lee3,
Sung Wook Park1†, Daesik Kim4, Jin Hyoung Kim1, Jin-Soo Kim4, Seokjoong Kim2, Jeong Hun Kim1,5,6‡, Jung Min Lee2,7‡

https://www.youtube.com/watch?v=uCpO-MjcnyY&list=PLREdUWqkOWWkQwqN9r3woCvuWKWiG1LGX